Pipeline
Pipeline Consisting of First-in-Class Peptide Therapeutics Focused on Hard to Drug Targets in Neuroscience
- Note:
- Amyotrophic Lateral Sclerosis (ALS), Frontotemporal Lobar Degeneration (FTLD), Facioscapulohumeral Muscular Dystrophy (FSHD) and Inclusion Body Myositis (IBM)
- Interference peptides: block protein-protein interactions
- Bi-functional Degraders: block the protein signalling pathway and degrade the disease causing protein